HIV PR inhibitors: Most enzyme inhibitors are

peptide-mimicking compounds that are transition

state analogs. In other words, these compounds

resemble the transition state configuration of the

natural substrate of the HIV PR. As a result, the

inhibitors bind the enzyme much more tightly than the

natural substrate (since the substrate must be

distorted in order to assume its transition state

configuration). These compounds are therefore

competitive enzyme inhibitors, which are classified

according to the symmetry of their structures. For

example, Merck's inhibitor, Indinavir, and Roche's

inhibitor, Saquinavir are not symmetrical, while

Abbott's ritonavir has a high degree of symmetry.

HIV PR inhibitors: Most enzyme inhibitors are

peptide-mimicking compounds that are transition

state analogs. In other words, these compounds

resemble the transition state configuration of the

natural substrate of the HIV PR. As a result, the

inhibitors bind the enzyme much more tightly than the

natural substrate (since the substrate must be

distorted in order to assume its transition state

configuration). These compounds are therefore

competitive enzyme inhibitors, which are classified

according to the symmetry of their structures. For

example, Merck's inhibitor, Indinavir, and Roche's

inhibitor, Saquinavir are not symmetrical, while

Abbott's ritonavir has a high degree of symmetry.

In the structure shown here, indinavir has replaced the

substrate. Indinavir is in red, and the active site Phe

residues are in white:

Drug resistance: Genetic resistance of HIV-1 strains

to protease inhibitors can occur. In the case of

indinavir this is mediated by in large part by a key

mutation at amino acid residue 82 (V82 -> A, F or T).

As above, indinavir is in red, and the active site Phe

residues are in white. Valine 82 is shown in yellow:

Importantly, viral mutations which confer resistance to

several of the other protease inhibitors are NOT the

same as those which confer resistance to indinavir.

For example, the key resistance mutation for

saquinavir maps to amino acid residue 90 (shown in

yellow; the active site Asp residues are in white):

Likewise, the key resistance mutation for nelfinavir

maps to amino acid residue 30 (shown in yellow; the

active site Asp residues are in white):

Other concerns/problems: An addition problem

with protease blockers is their oral bioavailability.

This has been a major problem in their development

(in many cases, 5% or less of ingested drug reaches

the circulation). In addition, the ability of these drugs to

enter the central nervous system (ie, to cross the

blood-brain barrier) appears to be quite limited in

many cases.

For more information, see Erickson and Wlodawer,

Annu. Rev. Biochem. 62:543-585, 1993.